curing via genetic materials
gene therapy
to repress a gene or deliver a gene missing in a patient?
if you can start from the gene, the gene produces the intended protein
GOI = gene of interest
and you need to use a vector (a virus….. etc)
vector could be anything, but the goal of it is to hsot the GOI
the red gene is defective
what we try to do is replace the gene with a healthy one
sometimes we do alot?