curing via genetic materials


gene therapy

to repress a gene or deliver a gene missing in a patient?

if you can start from the gene, the gene produces the intended protein

GOI = gene of interest

and you need to use a vector (a virus….. etc)

vector could be anything, but the goal of it is to hsot the GOI

the red gene is defective

what we try to do is replace the gene with a healthy one

sometimes we do alot?